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Category:All HeadlinesWorld & GeopoliticsMarkets & EconomyTech & AIPoliticsSearch results for: "FDA Approves Zilganersen," (30 stories)

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FDA Approves Zilganersen Injection, First Drug for Alexander Disease
Lead StoryPharmacy Timesgeneral
Sep 3

FDA Approves Zilganersen Injection, First Drug for Alexander Disease

<a href="https://news.google.com/rss/articles/CBMipAFBVV95cUxOSXBwTkUySEZyeW9SZDNKOFZYcVFJWWlUN0VMQkNqbV9ib2cyU1cySHBaY0YyLXBQNE56VnJzMFhTQmdFUHR4WjNZcUJULWJKajdJUkt3emRxWnpsb09ESnY1aWhKNG9RT3U3Z3dtWV9fMWt3QmVoUHVfRXFXTFYxSllsWnk5RlhSelBUcXR4SXpfOTFpbzZBSWg0RUtJbXItLVBBaw?oc=5" target="_blank">FDA Approves Zilganersen Injection, First Drug for Alexander Disease</a>  <font color="#6f6f6f">Pharmacy Times</font>

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Search Results for "FDA Approves Zilganersen,"

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29 stories displayed
FDA Approves Zilganersen, First Treatment for Alexander Disease
NeurologyLivegeneral

FDA Approves Zilganersen, First Treatment for Alexander Disease

<a href="https://news.google.com/rss/articles/CBMimAFBVV95cUxQMjFOV1dfQTJ2TDlhTU50eXNXR3ZNeW5Bb0Q5WDg4azV4aFZuUlpXQUlRU014WDh6U19vRkd2NVpmRnA0aURkSEk5S0Z1U3FxTFFHTVR0U09fLXFhZWxrSXJUdmxnYW1jOFZpcV82bG54V21wYzJHUE5EYUFzNERNMU9qb2JKbTFfb21LMEpabTBIcmdBN0FvMQ?oc=5" target="_blank">FDA Approves Zilganersen, First Treatment for Alexander Disease</a>  <font color="#6f6f6f">NeurologyLive</font>

FDA Approves First Disease-Modifying Treatment for AxD
The American Journal of Managed Care® (AJMC®)general

FDA Approves First Disease-Modifying Treatment for AxD

<a href="https://news.google.com/rss/articles/CBMihwFBVV95cUxQNi0yRWRIcWE5Wk5aSmdqOXNOblliRU5FcDNTekRsRVVNaDNLZFhFV25iS3Fva05LM2pKUmpqVGd6WjFCQkRlSmYwbUtPWE5adTNFVXRJMldGTGFrM19jS1VSTzVCVk9mTjMxbkZLR1VHcXp4THNSRGprd0pnYWh2VmtWVWRaM2s?oc=5" target="_blank">FDA Approves First Disease-Modifying Treatment for AxD</a>  <font color="#6f6f6f">The American Journal of Managed Care® (AJMC®)</font>

ZANVASTRO™ (zilganersen) approved by the FDA as the first and only disease modifying treatment for Alexander disease (AxD) in pediatric and adult patients
Business Wiregeneral

ZANVASTRO™ (zilganersen) approved by the FDA as the first and only disease modifying treatment for Alexander disease (AxD) in pediatric and adult patients

<a href="https://news.google.com/rss/articles/CBMirwJBVV95cUxNTml0eWpaOGFTTWN6Z29UOFIwVmpEbHpfSU9HU0dsZVF0RUJMS1NqTVdZc19CT1hEMVV4cXNsUnJ5aGREaE9VM1RmSzlGaEo5cFJKSHBCRnVIM0NlendWaXI5bXFVUzBaRGVHVERWMmoxNEE3SnNTSHVYdE5teWwyMk5BMXVCSWRiZVVqMHJvUFRzTGI4WmsyU2ZFS3gxZzdmZndLYm9leGQ4ZXd4V0lKT3hqM09yYngyR3pDSnFEaHRoYjVpUnEtQ3ZLQlRaZUhVVG9uNEt6U05CTHhITkJTLXpvWG9hZmNfdmJuMl9YcmZLTGhSRHczVWlNSWllVU5DeVpSQzE1NU53VDNlczFNR0NKRkJHOXMwcDNhYjJjcGRqc2d6a19hVEdDTnhKUE0?oc=5" target="_blank">ZANVASTRO™ (zilganersen) approved by the FDA as the first and only disease modifying treatment for Alexander disease (AxD) in pediatric and adult patients</a>  <font color="#6f6f6f">Business Wire</font>

FDA Approves Ionis Pharma Drug, the First for Ultra-Rare Alexander Disease
MedCity Newsgeneral

FDA Approves Ionis Pharma Drug, the First for Ultra-Rare Alexander Disease

<a href="https://news.google.com/rss/articles/CBMiyAFBVV95cUxNdWwzcU9ZMzM1dURuS3VqMTRfSkxZdlNYQWpRZkpKcER0aFEzUkx4aG9rbWV0ZkdnNlpEZVg2dGhHcVBZNDVFQkpnR19zY1NqM29jdk1SdnNrNWtRaGphbFZmQjhPMERGRmItZGh5bk8zUkF4M3pCMlpOZUVsRWJzVGRfaDNRWTlZRE5FVjVwbDJHNWk4ZWpTY05jWDBKUEw1bS1pRnFudzVNdVF1QWw3S0NsenFKNDlaanlVb2FqeE5acDdramlmWQ?oc=5" target="_blank">FDA Approves Ionis Pharma Drug, the First for Ultra-Rare Alexander Disease</a>  <font color="#6f6f6f">MedCity News</font>

FDA approves Ionis’ antisense drug as first targeted therapy for Alexander disease
BioSpacegeneral

FDA approves Ionis’ antisense drug as first targeted therapy for Alexander disease

<a href="https://news.google.com/rss/articles/CBMirwFBVV95cUxNX0FEU1FDTktMQ0FrNTBiOURiU1VGQWdLZDMwZ2tjVDZ1a0I2Sm81aFVTS0lmM3preDdrLUpGVS1HQml0NjNHNWpyV083VEk5UkwzaU1yQjgydy04WkV6RmVaU2tNRGVyX29mVHRFMXZFMjVVSG1objNkWWhpWE1iQ0VLVFNFZ1JHQmVtSUhkWUxDNFJMTnREcUQwaVU3dFhiVVZteXNfdzVZYU02Mlhz?oc=5" target="_blank">FDA approves Ionis’ antisense drug as first targeted therapy for Alexander disease</a>  <font color="#6f6f6f">BioSpace</font>

FDA Approves Zanvastro for Alexander Disease in Pediatrics & Adults
Pharmaceutical Executivegeneral

FDA Approves Zanvastro for Alexander Disease in Pediatrics & Adults

<a href="https://news.google.com/rss/articles/CBMikwFBVV95cUxPSklmb29YeklxenRxa1lCVnVDdTlhTmFITDFFbXkyVklUWlZGRVZCcEtpTnpwV0pxeWJ5RGlzWlRBY2tWRU0xTHZScUxzcU1rc2s1TGk4TTdLVklJLXpQODMxczI5cUNIbFNBSFhQMGZUc2VQTEhlZmtEb0p2QzE2Y2F1dEVfTkR0X2doeXVWSExxWlE?oc=5" target="_blank">FDA Approves Zanvastro for Alexander Disease in Pediatrics & Adults</a>  <font color="#6f6f6f">Pharmaceutical Executive</font>

Rare Brain Disorder Gets Its First FDA Drug Approval
MedPage Todaytech

Rare Brain Disorder Gets Its First FDA Drug Approval

<a href="https://news.google.com/rss/articles/CBMib0FVX3lxTE84UEJNUzQ1d0pGMGp0am16aUszUFJ6V0pfMUphVk5XZkFiVmlrSjEtUmV6NGxWc2FVQXBIbWxqV0d2NWU4eHJrMXRSMXVzTXRaeEJhOGxWUkViOHZkVUFQYjM5TWRKU1l3YkJ3NnlKTQ?oc=5" target="_blank">Rare Brain Disorder Gets Its First FDA Drug Approval</a>  <font color="#6f6f6f">MedPage Today</font>

Ionis wins FDA clearance for Alexander disease drug, company's first solo neurology approval
Endpoints Newsgeneral

Ionis wins FDA clearance for Alexander disease drug, company's first solo neurology approval

<a href="https://news.google.com/rss/articles/CBMijgFBVV95cUxPbzd1cGpyY1ZOaVVNSE9vTmVQSUZUbWxNWDRxZGtNZUptalBpZHNLcW9pZzdjRjJmUVFEVVU2RWNNZWNJY19IVFZxdUVZZm5Pd21Ua0V1U1BtTnVSSHVocG5YRXVEWVVwTmtyVHF0LWhaeFp3bVNFd0tjU1NhY3JxZ08tN0M5Z3JtekczVWx3?oc=5" target="_blank">Ionis wins FDA clearance for Alexander disease drug, company's first solo neurology approval</a>  <font color="#6f6f6f">Endpoints News</font>

Ionis’ ‘breakthrough’ Alexander disease approval establishes pillar of rare disease pipeline
Fierce Pharmageneral

Ionis’ ‘breakthrough’ Alexander disease approval establishes pillar of rare disease pipeline

<a href="https://news.google.com/rss/articles/CBMivwFBVV95cUxQVDV5T3Uyejlxa2VUaEdvaUJKVDFoM3FQVEtZZkU3WldfZkNxLVRuWGRPS1hOeTZrcENaYmFRazBLdWpBc0N2WUNwZk12Nm5mQUU3Y3kwanhpWmxXRkZqaXZfR25FYW9JaDRlRHNKV3QwVUJUcWtnSW1GNU1SZnpWSXhMd1hxSlpwTllsRVdmWmdWZFdvdWlmOUNOVEY3aC0tTUtmR21oR0JSaWlIZHNhUXFlejZjakQ0eW04Tks1cw?oc=5" target="_blank">Ionis’ ‘breakthrough’ Alexander disease approval establishes pillar of rare disease pipeline</a>  <font color="#6f6f6f">Fierce Pharma</font>

What an Alexander Disease Approval Means for RNA Developers
PharmTech.comgeneral

What an Alexander Disease Approval Means for RNA Developers

<a href="https://news.google.com/rss/articles/CBMilAFBVV95cUxQN2RwVGFJMGxGWVZkQ2RhMGYzMGRCb3I3ZnRLZldjdmhZaVM5YWNROTVsVy1IZkx1RTJMNHJaWmQySWtfWUtIdXNUMV9LR1l4RlNRNkhFeXpsTnN6ZHRiT2s5NmNDVVhHckRmbUltZlZ0amVpZGQtYkFfYy0xNk1hQWxWdGJGTGQ4VVZRSmlzelBuMUky?oc=5" target="_blank">What an Alexander Disease Approval Means for RNA Developers</a>  <font color="#6f6f6f">PharmTech.com</font>

Ionis gains approval of zilganersen for Alexander disease (NASDAQ:IONS)
Seeking Alphatech

Ionis gains approval of zilganersen for Alexander disease (NASDAQ:IONS)

<a href="https://news.google.com/rss/articles/CBMilAFBVV95cUxOWkdmcy0tdVpuWFpvZ0RIVDBYMm9nQW5WMkZuMmtvQzlSc0FoenZ1WEVXS1phRGhTT3dUajRIOE5IQUpEQXZWdHlWcUJ5cWVRTEE4a05aQnY1eUJiMmlUUjdrLXMycXA0bW9IT0xjWmhwajhrZzFHc1NGNzVQVllMWmlwSUtkM0VDWTZNV0c0REd5ckM3?oc=5" target="_blank">Ionis gains approval of zilganersen for Alexander disease (NASDAQ:IONS)</a>  <font color="#6f6f6f">Seeking Alpha</font>

FDA approves Zanvastro as first disease-modifying treatment for Alexander disease
AllScigeneral

FDA approves Zanvastro as first disease-modifying treatment for Alexander disease

<a href="https://news.google.com/rss/articles/CBMigAFBVV95cUxQVW9UQTMta0x3czd4Sjk5allrd0lGLWtKSkx3c0syS2ZweThmdEYwZmg3eElfUk50SUhDeWdyOVRuS3VYblBJR3hTcnpuZExFTXk4ZzlHcnBlQU1oM0ZMQnZGWHYtUzZOcFdBVnlHQ3dvbk1RbDloaF9YSTdWdElqYg?oc=5" target="_blank">FDA approves Zanvastro as first disease-modifying treatment for Alexander disease</a>  <font color="#6f6f6f">AllSci</font>

Ionis bags $30M from Recordati for ex-US rights to near-approval rare disease prospect
Fierce Biotechgeneral

Ionis bags $30M from Recordati for ex-US rights to near-approval rare disease prospect

<a href="https://news.google.com/rss/articles/CBMisAFBVV95cUxOWXdwY0ZfNTlZMVlnZWNiZTRGTzRyZjRPZzVEamswTThvVTM0b2Z4OGRCQm91MGlqZkVFUlFuSk4zdnNwdkM3UmJ5a1EzTUdLUGVPQlRHa3JBalpRSVpCZlRRSDJPTy1SNmZBNzNINnZXb0RFRUUtcUp5ZDM4eUtPdU52RVpHMzIxT1J6dmZsckRiOERIZ1hJZjFDcnNjR1paVTkxWkdOTGN0QlpWZnJRcA?oc=5" target="_blank">Ionis bags $30M from Recordati for ex-US rights to near-approval rare disease prospect</a>  <font color="#6f6f6f">Fierce Biotech</font>

Clinical Considerations and Impact of Newly Approved Zilganersen for Alexander Disease
NeurologyLivegeneral

Clinical Considerations and Impact of Newly Approved Zilganersen for Alexander Disease

<a href="https://news.google.com/rss/articles/CBMirwFBVV95cUxNM2c4UldsZXNaV3drTVQtYjdSWElFXzVKOTNDclNTTVphaTRHWUdJX0FPZTA5QUV5OFpmdWZ5ekVveF9NWTk0WVUtRi1JYnRscjJHcU5YVm5nM2dET3ktQk9VQ3RaNkF5bUZ0YkZIR3M0bWJDdWNiVkRSekdBcmNrOVJUdXBOX3VWdlVoMEYyMXI2MDkzOGtwcGdSZWdLNDQ4aGswbEJrRFdRUlBRS0Qw?oc=5" target="_blank">Clinical Considerations and Impact of Newly Approved Zilganersen for Alexander Disease</a>  <font color="#6f6f6f">NeurologyLive</font>

Ionis wins FDA approval for Zilganersen to treat Alexander disease
Indian Pharma Postgeneral

Ionis wins FDA approval for Zilganersen to treat Alexander disease

<a href="https://news.google.com/rss/articles/CBMitwFBVV95cUxNd2JaeGZseHB1c2taZzNBb1gwSHA4MEpfRHRFZ2c5enpJUTlKYkk4c0s5Z2xUUm43V1BUQTF4dFV3Zm03b2ViX2U0WHg0WFNsVFBEYzlmWEl1QzZMMjljYjktWkQ0dXVhNU96R1EzV0hXeURnXzJpWHlRUE02aWpacjVNR3dFTFFHbTJVRVFwTDRRY0NZTWpCazQzSWRxcGhmUWhmQlV4dll1NllFQkQtMTV3aWZrVW_SAb4BQVVfeXFMTmh4Z0RCdmRQN1BrU3dDY1g2Xy12T1Jjd1lQaEV1UmZ0bHJMLXQxemRneVB0SGJlNS1RdnZfTHlsS19UUmFuTHpBUzhiLUV2cFJkam1pRzRpd19QUENpRFpwVWY4VTVBdFViYzVMdWc4RU83TnNoRVJXczFiaDdZVV9HVTZyQkd1a2ZjOFlVeGVkN1lPMG1IWXMzYnVXVlBmaDU2Y2ZwbTR5aERLaHFtMVlmU1FwQlNyb19XaHh4QQ?oc=5" target="_blank">Ionis wins FDA approval for Zilganersen to treat Alexander disease</a>  <font color="#6f6f6f">Indian Pharma Post</font>

Ionis Pharma prices first FDA-approved treatment for Alexander disease at $285,000 per dose
Reutersgeneral

Ionis Pharma prices first FDA-approved treatment for Alexander disease at $285,000 per dose

<a href="https://news.google.com/rss/articles/CBMitwFBVV95cUxNOEY3cUliaWZpa0d5UkpjQTdGZnNMNlFjX09yTmJOUHhrc2VoNnM0ZENubGFCcGZWYndnX3pETDE0dWVlRkxfVGxGU2t3VU9HY1plaE1IZUl1ZmNsZFZTdlJxTnNSd1JVZGpTcEs3eXFkWktxbkxtdUpmM0xfR09wcE1jLWU2ZEJsOVAyWlk4WGxfMWJfU19pMERnajRqUzA0UGhoUUtNd2pWY1liU1V6cnlmSGFsbUU?oc=5" target="_blank">Ionis Pharma prices first FDA-approved treatment for Alexander disease at $285,000 per dose</a>  <font color="#6f6f6f">Reuters</font>

FDA Accepts Zilganersen New Drug Application for Priority Review in Alexander Disease
NeurologyLivegeneral

FDA Accepts Zilganersen New Drug Application for Priority Review in Alexander Disease

<a href="https://news.google.com/rss/articles/CBMiswFBVV95cUxOVlBXbnBTZ0ZVSjNxdzU3cXRTUVlHTDdvWG9XV09RNkd1MGlnQkxBMzRmVUZBaXoxUG9XTFVRU2xwTDZxNTBjTTZaLWlNV1l2NTdYbnpiX0FQLVdmUmlqU2hXOEowWUVoNmhZcFBTZk1CdDZRQXBMR2I5SUFGeDg3UHg4bm0zVW5DVUo4RDZQQ3lNMWcyNFd3b2xyME13TGxNTVVXalZGRV9VTnMxZGVRTFNMdw?oc=5" target="_blank">FDA Accepts Zilganersen New Drug Application for Priority Review in Alexander Disease</a>  <font color="#6f6f6f">NeurologyLive</font>

New Ionis drug gets FDA greenlight for rare brain disorder
EMJtech

New Ionis drug gets FDA greenlight for rare brain disorder

<a href="https://news.google.com/rss/articles/CBMioAFBVV95cUxPdlN5YWVZcEhoZHFsRkdULUt3Qy1zQ3VQZFllbDctLXctUXdtejJlQm5HWFR2aUpfNmxTd0QwUVYtTndIeW05dGpkZVpVbHhsbDFmaUpJcHMxNXFIUHYzWlpBcUVJeVZnT2E5R3A0YWZxSnJqWmRhUjVtUlFrX1d4VHEyaEgwamlKem9jc3pnLTNPTm1PaVNIUFQzSFlsYjZl?oc=5" target="_blank">New Ionis drug gets FDA greenlight for rare brain disorder</a>  <font color="#6f6f6f">EMJ</font>

First Disease Modifying Treatment for Alexander Disease Approved
Neurology Advisorgeneral

First Disease Modifying Treatment for Alexander Disease Approved

<a href="https://news.google.com/rss/articles/CBMilgFBVV95cUxPUnBJT3F3a1lyR0tsMGFRQnI0VFRuSXRvbFJUYnBaTTZaX09EbWttT3RyaHMyakhPMlJ5dWhOU01wRXVKMnJRUXkwRmJrRzJGNkpfQVdtckpGQ3FnZWZSOUpBOE9lNWtrZlNvWGdsZmVLZU1uUVJiam9JZHVxdkIzRW9UUC1ZemU5bmtEYnRWZndBdmNzcFE?oc=5" target="_blank">First Disease Modifying Treatment for Alexander Disease Approved</a>  <font color="#6f6f6f">Neurology Advisor</font>

Ionis announces zilganersen New Drug Application for Alexander disease (AxD) accepted by FDA for Priority Review
Business Wireworld

Ionis announces zilganersen New Drug Application for Alexander disease (AxD) accepted by FDA for Priority Review

<a href="https://news.google.com/rss/articles/CBMi-wFBVV95cUxObWdwcndOdVl0Y29yanZ6UUtLdWE0Xzd2R3I5MDlvQkNUVWhfLTJtcWc1bGhyVDdHOVk0SlVVMmExRFprS1BoOXNtT3p4QUU0dTBueHF0RGFDYWhWZzZfd2d5bkFKQVZMWjNtelV1Vl96dXgydDlWVmFTTmRDSU5UU1NST2UzdVN2RU85djMtN3JXMHBkTDE2U2pYRFZzTFYxUlZPZHYxb2EyeW4wYzU3aXd5clE0dW9iTUt6Zm5XOXN4OFpIcmd6Ny1jZ3M4Z3owRUpMQjJDUkhsUVl4N1U4ZlplYjlyWkpKUHhkTHY5QkpvMWZwd2Rja2Rvaw?oc=5" target="_blank">Ionis announces zilganersen New Drug Application for Alexander disease (AxD) accepted by FDA for Priority Review</a>  <font color="#6f6f6f">Business Wire</font>

Ionis announces license agreement with Recordati for zilganersen in Alexander disease (AxD) in all countries outside the U.S.
Business Wireworld

Ionis announces license agreement with Recordati for zilganersen in Alexander disease (AxD) in all countries outside the U.S.

<a href="https://news.google.com/rss/articles/CBMijAJBVV95cUxOSGJNUTBOTFkzVTdDaUM0T1VtTHJNTlhUaXdTbzFhVlc1cmFVVmI2UEY2WE5yNlI0Q185MTVTWW5mY3hMdnoyQzlON1l3UG5TcjlncFlaRDZPUFJuRHlwUExRVk9KRm05dktlODR2Y0V2Z29qcnhuZ1FVdjd5WkFMdC12S0tqSWZSWHRQeUoyS3VSWGNCbzhEeWU1UEdIbkljbmNkZWRndGlJNFVEdXVjbWZ1RnVuaktDN3hIcm1ZY3VfT1JDcmwyX1VONEh5akgzbVUtN0RPWmpnVm9paHVuZTFCU2hVbkdFZnAyTF9Mbi0zQ3BjanlHWENhWDVDaWl0a1NYdm5Wb29EM0ls?oc=5" target="_blank">Ionis announces license agreement with Recordati for zilganersen in Alexander disease (AxD) in all countries outside the U.S.</a>  <font color="#6f6f6f">Business Wire</font>

FDA Drug Approval Decisions Expected in September 2026 - MPR
Medical Professionals Referencegeneral

FDA Drug Approval Decisions Expected in September 2026 - MPR

<a href="https://news.google.com/rss/articles/CBMiaEFVX3lxTE1ORzFWUTlEbTlUbElzbjI2MkNEV1djR2FsWmQxRllubjBRNGxQX19nS0ZmQTVIVkFkZS1xdjRLeDlMalE2VFozYUtEWDgzRVdGQW83TTJOaktXUW82akwyNHM1Vlg0TGlm?oc=5" target="_blank">FDA Drug Approval Decisions Expected in September 2026 - MPR</a>  <font color="#6f6f6f">Medical Professionals Reference</font>

Ionis’ ASO for ultra-rare neurological disorder awaits FDA’s decision
BioXconomytech

Ionis’ ASO for ultra-rare neurological disorder awaits FDA’s decision

<a href="https://news.google.com/rss/articles/CBMiqgFBVV95cUxOQUF3Zzg3cTg0VXYxWUt4YV8tc0lOWU5rM2N6OWFUNDhyMXhuZno3VXBRa1lWWEdGRVBQaExycHAybktRQ3cwWTZPVHk4dWFFY29tNnlIM0xVRmdDekFhNVplbEEtY1FGRDZLNWZldkY1aG5wVEdUTlBkX2Z1LWk3eWZzYklxVVEyTUVxUmJhNHhBOEpPTUlTNW45MlBaRHVKQTBhUm9JTVUxZw?oc=5" target="_blank">Ionis’ ASO for ultra-rare neurological disorder awaits FDA’s decision</a>  <font color="#6f6f6f">BioXconomy</font>

Ionis plots FDA filing after rare neurological disease candidate posts phase 3 win
Fierce Biotechgeneral

Ionis plots FDA filing after rare neurological disease candidate posts phase 3 win

<a href="https://news.google.com/rss/articles/CBMisAFBVV95cUxOejBubEE2VVJVdFVZa01henNXMzlYTHkyWTRsWXJLaE9mU1VxVXJDR1lvMXdFVVZpV3BHNk5kSm83d3FYODhtVHRvQ1RSczBQVDdtY2FGNUdOV2RGZXJQdTBuNGZlWmZhcU93VFV0MXJpamZ3STJFSXM2MmpsSlM3dnBhQkFhVFZtSlJQSHVsRmRfUWFESVRaVk5lT2YzdzhoQTdFYWF5OWtvbUdZaXU3Vw?oc=5" target="_blank">Ionis plots FDA filing after rare neurological disease candidate posts phase 3 win</a>  <font color="#6f6f6f">Fierce Biotech</font>

Ionis’ antisense drug stabilizes ultra-rare disease ahead of FDA decision
BioSpacegeneral

Ionis’ antisense drug stabilizes ultra-rare disease ahead of FDA decision

<a href="https://news.google.com/rss/articles/CBMitAFBVV95cUxNc0FoeUdnQTB3c0RsUHY3UktGQk9SYTh2TmlhVWUtZWs4M0RpUjV1UzNLVWgzQ1B3bktYUFF4MFFJZFlVQS1VSEJUUUNuSkhoVUFGZWp2LXBoZlE5dVNJVWlubVdiZDFYSzdGcXVZZ19rYXAwbUNkWlFSNVZsbDlQaUFlNFlSUGdFcFR0Y3hLcXJSdVoyTTF2YVZSeThIZzd6bG8zUGxlMlNzOGxHNm1lU3BKdWc?oc=5" target="_blank">Ionis’ antisense drug stabilizes ultra-rare disease ahead of FDA decision</a>  <font color="#6f6f6f">BioSpace</font>

Ionis Plans Application Submission for Zilganersen as Potential First Treatment for Alexander Disease Following Positive Data
NeurologyLivegeneral

Ionis Plans Application Submission for Zilganersen as Potential First Treatment for Alexander Disease Following Positive Data

<a href="https://news.google.com/rss/articles/CBMi4wFBVV95cUxOOTdCQmFlTWlKOE9sdzVsV0R6c3hjUHlNN2pHcS1FV3hHN0owQk1oaHAxcS1lVU5KVHB5cy11NkI0UU1uNHF4OVdBNHNMelFZcU5EOTZvOVl5QmI5eVRXRE9zYUxyRzVlM25WQmVhUXlvc1NXbkIwQ05LdHdZWjhyYjh5UHZaR05LUzZtX19uLVlVc1FhZ2N3WnJtUkwxbDBYbm5zdlBzMkt1UmFGY3pEVnlmQUV1SXlEcnZUcm5LYmhxYUZvcXJ1Wjk4MG5tNnlfUmZCbXM3U0NmUENXOE9ra3NhWQ?oc=5" target="_blank">Ionis Plans Application Submission for Zilganersen as Potential First Treatment for Alexander Disease Following Positive Data</a>  <font color="#6f6f6f">NeurologyLive</font>

Ionis says RNA drug for rare brain disorder succeeded pivotal trial, plans to ask for FDA approval
Endpoints Newstech

Ionis says RNA drug for rare brain disorder succeeded pivotal trial, plans to ask for FDA approval

<a href="https://news.google.com/rss/articles/CBMivgFBVV95cUxPejNGTEZ4RXZBaXJ4QjUxTWh5UUR0dkxraEpHQ2IwMUZQc3JMbWgwWVY1dW9rVGRCNG1aWWVJeEFKM2ZjZTlpWlFVdTQtSVgwZTVoZGFDU0dmZnI0dmdYRHRFdTAzQkdOZ1ItTFplQWhPWWRqay1fTVhtWExGVjZTV0RzNEZ5SllFV2pnb1pSUTgwRzJidzQzVlZNVU1RSGpjOWVpYkV3eUQwRmE2ZGFuX0dTZW5tY2hweE1EQUVR?oc=5" target="_blank">Ionis says RNA drug for rare brain disorder succeeded pivotal trial, plans to ask for FDA approval</a>  <font color="#6f6f6f">Endpoints News</font>

The Broader Lessons From Zilganersen's Path to Approval
NeurologyLivegeneral

The Broader Lessons From Zilganersen's Path to Approval

<a href="https://news.google.com/rss/articles/CBMijwFBVV95cUxPbVhPOTl0d1d3VFFpTXFJY1hVNFVzb2ZxamlPUG5sMFFIcVFuWEdhMkxkdEJ6dU5kYkFnNURBSFhUZ2lfaHhqQ1JXZkpDdjJNT01HRi1DTFBJNU1MT2FRVWR3eUh1czJiUmZOQmxYRGlaRUVqdDVYdVpuQ0l0dFIwSmpsMFZxRXBXV2JuMkxtUQ?oc=5" target="_blank">The Broader Lessons From Zilganersen's Path to Approval</a>  <font color="#6f6f6f">NeurologyLive</font>

Ionis Heads to FDA as Antisense Therapy Aces Pivotal Study in Rare Neurological Disease
BioSpacegeneral

Ionis Heads to FDA as Antisense Therapy Aces Pivotal Study in Rare Neurological Disease

<a href="https://news.google.com/rss/articles/CBMiyAFBVV95cUxQb1dYVjlud1h3VEgtQ2kxMDRUb3BiVWFRaV9zOHpFN2lkSE05azVsLUx0X0R0Z2NlaWowVTZacE1GRFBLZUszaWVHWjdqRzJ6SGpZeFNiY25naUVNRlpYRWpqTzFMMndKVENBMUlIS1MzSEdPMGsteFJuX0ZkV0hPOERHdlZzRG04Q3A2d2xUZjlPYXJOQVZXZW1vUFR0clpOZWNMYVFsWXRSa3lDVXE3NjQ1NjItb0s0a3hDRkZvRjBENk10dzE2bQ?oc=5" target="_blank">Ionis Heads to FDA as Antisense Therapy Aces Pivotal Study in Rare Neurological Disease</a>  <font color="#6f6f6f">BioSpace</font>

"FDA Approves Zilganersen," — Live Google News Trends & Headlines